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Muscular dystrophy, Duchenne and Becker types
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DBMD; Duchenne/Becker muscular dystrophy
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Muscular dystrophy, Duchenne and Becker ... Clinical Trials
- Molecular Analysis of Patients With Neuromuscular Disease
ClinicalTrials.gov Identifier: NCT00390104 - Recruiting
Limb-Girdle Muscular Dystrophy; Duchenne Muscular Dystrophy; Becker Muscular Dystrophy; Facioscapulohumeral Muscular Dystrophy
- Gentamicin Treatment of Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00005574 - Completed
Becker muscular dystrophy; Duchenne muscular dystrophy
- Safety and Efficacy Study of Antisense Oligonucleotides in Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00159250 - Recruiting
Duchenne Muscular Dystrophy
- High-dose Prednisone in Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00110669 - Active, not recruiting
Duchenne Muscular Dystrophy
- A Safety Study in Adult Muscular Dystrophy Patients
ClinicalTrials.gov Identifier: NCT00104078 - Completed
Becker Muscular Dystrophy; Facioscapulohumeral Muscular Dystrophy; Limb-Girdle Muscular Dystrophy
- Safety Study of Mini-Dystrophin Gene to Treat Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00428935 - Active, not recruiting
Duchenne Muscular Dystrophy
- Study of Daily Pentoxifylline as a Rescue Treatment in Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00243789 - Active, not recruiting
Muscular Dystrophy, Duchenne
- KUL0401: An Open-label Pilot Study of Oxatomide in Steroid-Naive Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00033813 - Completed
Muscular Dystrophy, Duchenne
- Safety and Efficacy Study of PTC124 in Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00264888 - Active, not recruiting
Duchenne Muscular Dystrophy
- Six Month Study of Gentamicin in Duchenne Muscular Dystrophy With Stop Codons
ClinicalTrials.gov Identifier: NCT00451074 - Recruiting
Duchenne Muscular Dystrophy
- Biomechanical Analysis of Gait in Individuals With Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00312247 - Recruiting
Duchenne Muscular Dystrophy
- A multicenter randomized placebo-controlled double-blind study to assess efficacy and safety of glutamine and creatine monohydrate in Duchenne muscular dystrophy (DMD)
ClinicalTrials.gov Identifier: NCT00018109 - Completed
Muscular Dystrophy, Duchenne
- An Open-label Pilot Study of Coenzyme Q10 in Steroid-Treated Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00033189 - Completed
Muscular Dystrophy, Duchenne
- Pentoxifylline in Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00102453 - Active, not recruiting
Muscular Dystrophy, Duchenne
- Creatine and Glutamine in Steroid-Naive Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00016653 - Completed
Muscular Dystrophy, Duchenne
- Effect of Oral Glutamine on Muscle Mass and Function in Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00296621 - Completed
Muscular Dystrophy, Duchenne
- Phase III Randomized, Double-Blind Study of Prednisone for Duchenne Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00004646 - Completed
Duchenne Muscular Dystrophy
- CoQ10 and Prednisone in Non-Ambulatory DMD
ClinicalTrials.gov Identifier: NCT00308113 - Recruiting
Duchenne Muscular Dystrophy
- A 5 Year Longitudinal Study of the Natural History of DMD
ClinicalTrials.gov Identifier: NCT00468832 - Recruiting
Duchenne Muscular Dystrophy
- Randomized Study of Albuterol in Patients with Facioscapulohumeral Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00004685 - Active, not recruiting
Muscular Dystrophy, Facioscapulohumeral
- Test-Retest Reliability of Pulmonary Function Tests in Patients With Duchenne's Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00207857 - Recruiting
Duchenne's Muscular Dystrophy; Scoliosis
- The Cardiovascular Genetic and Therapeutic Implications of Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00518817 - Not yet recruiting
Muscular Dystrophy; Dilated Cardiomyopathy; Heart Failure
- A Clinical Evaluation of FKRP Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00313677 - Recruiting
Muscular Dystrophy
- Myotonic Dystrophy and Facioscapulohumeral Muscular Dystrophy Registry
ClinicalTrials.gov Identifier: NCT00082108 - Recruiting
Myotonic Dystrophy; Muscular Dystrophy, Facioscapulohumeral; Muscular Dystrophy
- Study of Muscle Wasting and Altered Metabolism in Patients with Myotonic Dystrophy
ClinicalTrials.gov Identifier: NCT00004769 - Completed
Muscular Dystrophy
- Genetics of Cardiovascular and Neuromuscular Disease
ClinicalTrials.gov Identifier: NCT00138931 - Recruiting
Cardiomyopathy; Arrhythmia; Muscular Dystrophy
- Genetic Characterization of Individuals With Limb Girdle Muscular Dystrophy
ClinicalTrials.gov Identifier: NCT00457912 - Recruiting
Limb Girdle Muscular Dystrophy
- Gene Transfer Therapy for Treating Children and Adults With Limb Girdle Muscular Dystrophy Type 2D (LGMD2D)
ClinicalTrials.gov Identifier: NCT00494195 - Recruiting
Muscular Dystrophies
- Study of Inherited Neurological Disorders
ClinicalTrials.gov Identifier: NCT00004568 - Recruiting
Ataxia; Motor Neuron Disease; Muscular Disease; Muscular Dystrophy; Peripheral Nervous System Disease
- Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Types II or III
ClinicalTrials.gov Identifier: NCT00439569 - Not yet recruiting
Spinal Muscular Atrophy Type II; Spinal Muscular Atrophy Type III
- Studies of Patients with Skin Disease, Patients with Neurological Degenerations, and Normal Volunteers
ClinicalTrials.gov Identifier: NCT00001164 - Completed
Healthy; Muscular Dystrophy; Retinal Degeneration; Skin Diseases; Virus Diseases
- Molecular and Genetic Studies of Congenital Myopathies
ClinicalTrials.gov Identifier: NCT00272883 - Recruiting
Centronuclear Myopathy; Congenital Fiber Type Disproportion; Multiminicore Disease; Myotubular Myopathy; Nemaline Myopathy; Rigid Spine Muscular Dystrophy; Undefined Congenital Myopathy
- A Pilot Therapeutic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy
ClinicalTrials.gov Identifier: NCT00083746 - Active, not recruiting
Spinal Muscular Atrophy
- Effects of SomatoKine (Iplex) (rhIGF-I/rhIGFBP-3) in Myotonic Dystrophy Type 1
ClinicalTrials.gov Identifier: NCT00233519 - Active, not recruiting
Myotonic Dystrophy Type 1
- Study of Albuterol and Oxandrolone in Patients With Facioscapulohumeral Dystrophy (FSHD)
ClinicalTrials.gov Identifier: NCT00027391 - Completed
Muscular Dystrophies
- Measuring Levels of SMN in Blood Samples of SMA Patients
ClinicalTrials.gov Identifier: NCT00061607 - Active, not recruiting
Spinal Muscular Atrophy
- A Pilot Theraputic Trial Using Hydroxyurea in Type I Spinal Muscular Atrophy Patients
ClinicalTrials.gov Identifier: NCT00568698 - Active, not recruiting
Muscular Atrophy, Spinal
- A Pilot Therapeutic Trial Using Hydroxyurea in Type II and III Spinal Muscular Atrophy Patients
ClinicalTrials.gov Identifier: NCT00084006 - Active, not recruiting
Spinal Muscular Atrophy
- Valproic Acid and Carnitine in Patients With Spinal Muscular Atrophy
ClinicalTrials.gov Identifier: NCT00227266 - Active, not recruiting
Spinal Muscular Atrophy
- A Pilot Theraputic Trial Using Hydroxyurea in Type II and Type III Spinal Muscular Atrophy Patients
ClinicalTrials.gov Identifier: NCT00568802 - Active, not recruiting
Muscular Atrophy, Spinal
- Dutasteride to Treat Spinal and Bulbar Muscular Atrophy (SBMA)
ClinicalTrials.gov Identifier: NCT00303446 - Active, not recruiting
Kennedy's Disease; Spinal and Bulbar Muscular Atrophy
- Avastin for CNV Secondary to Pattern Dystrophy
ClinicalTrials.gov Identifier: NCT00391144 - Recruiting
Choroidal Neovascularization Secondary to Pattern Dystrophy
- Quantitative Analysis of SMN1 and SMN2 Gene Based on DHPLC System
ClinicalTrials.gov Identifier: NCT00155168 - Recruiting
Spinal Muscular Atrophy
- A Randomized, Double-Blind, Placebo-Controlled Trial of Hydroxyurea in Spinal Muscular Atrophy
ClinicalTrials.gov Identifier: NCT00485511 - Recruiting
Spinal Muscular Atrophy
- Study to Evaluate Sodium Phenylbutyrate in Pre-Symptomatic Infants With Spinal Muscular Atrophy
ClinicalTrials.gov Identifier: NCT00528268 - Recruiting
Spinal Muscular Atrophy
- Valproic Acid in Ambulant Adults With Spinal Muscular Atrophy
ClinicalTrials.gov Identifier: NCT00481013 - Recruiting
Spinal Muscular Atrophy
- Clinical Study of Spinal Muscular Atrophy
ClinicalTrials.gov Identifier: NCT00443066 - Recruiting
Spinal Muscular Atrophy
- Comparative Trial of Botox in the Management of Children with Congenital Muscular Torticollis
ClinicalTrials.gov Identifier: NCT00175604 - Not yet recruiting
Congenital Muscular Torticollis (CMT)
- Neurotropin to Treat Acute Dental and Chronic Neural Pain
ClinicalTrials.gov Identifier: NCT00006289 - Recruiting
Causalgia; Facial Pain; Reflex Sympathetic Dystrophy
- Safety and Efficacy Study of Recombinant Human Insulin-Like Growth Factor-I/Recombinant Human Insulin-Like Growth Factor Binding Protein-3 (rhIGF-I/rhIGFBP-3) In Myotonic Dystrophy Type 1
ClinicalTrials.gov Identifier: NCT00577577 - Recruiting
Myotonic Dystrophy Type 1
- RAMYD STUDY
ClinicalTrials.gov Identifier: NCT00127582 - Recruiting
Myotonic dystrophy type 1,; Sudden Cardiac Death
- Establishing Novel Detection Techniques for Various Genetic-Related Diseases by Applying DHPLC Platform.
ClinicalTrials.gov Identifier: NCT00154960 - Recruiting
Spinal Muscular Atrophy; Neonatal Hyperbilirubinemia; Colon Cancer
- Clinical Trial of Sodium Phenylbutyrate in Children With Spinal Muscular Atrophy Type I
ClinicalTrials.gov Identifier: NCT00439218 - Not yet recruiting
Spinal Muscular Atrophy Type I
- International SMA Patient Registry
ClinicalTrials.gov Identifier: NCT00466349 - Recruiting
Muscular Atrophy, Spinal
- Comparison of Two Lower Limb Bypass Types : Prosthesis Versus Autologous Vein
ClinicalTrials.gov Identifier: NCT00221715 - Active, not recruiting
Arteritis; Diabetes
- Novel Diagnostics With Optical Coherence Tomography: Imaging the Anterior Eye
ClinicalTrials.gov Identifier: NCT00343473 - Recruiting
Fuch's Dystrophy; Corneal Disorders; Subjects Who Have Had Refractive Surgery
- Combined Effects of Nutritional and Exercise Countermeasures
ClinicalTrials.gov Identifier: NCT00447044 - Recruiting
Muscular Atrophy; Muscle Weakness
- Botulinum Toxin for the Treatment of Involuntary Movement Disorders
ClinicalTrials.gov Identifier: NCT00001208 - Recruiting
Chorea; Drug Induced Dyskinesia; Movement Disorder; Muscular Disease; Tic Disorder
- Qigong vs. Aerobic Exercise in the Treatment of Childhood Chronic Musculoskeletal Pain
ClinicalTrials.gov Identifier: NCT00312234 - Recruiting
Muscular Disease; Fibromyalgia
- Clinical Trial of Vitamin E to Treat Muscular Cramps in Patients With ALS
ClinicalTrials.gov Identifier: NCT00372879 - Recruiting
Amyotrophic Lateral Sclerosis
- Effect of Increased Muscular Work During Different Weaning Strategies in Critically Ill Patients
ClinicalTrials.gov Identifier: NCT00538746 - Recruiting
Acute Respiratory Failure
- Retinal Imaging in Patients With Inherited Retinal Degenerations
ClinicalTrials.gov Identifier: NCT00254605 - Recruiting
Retinitis Pigmentosa; Cone-Rod Dystrophy; Macular Degeneration
- Transplantation of Tissue Cultured Human Amniotic Epithelial Cells Onto Damaged Ocular Surfaces
ClinicalTrials.gov Identifier: NCT00344708 - Recruiting
Corneal Epithelial Dystrophy
- IRIS PILOT - Extended Pilot Study With a Retinal Implant System
ClinicalTrials.gov Identifier: NCT00427180 - Recruiting
Retinitis Pigmentosa; CRD (Cone Rod Dystrophy); Choroideremia
- Efficacy and Safety of DHEA for Myotonic Dystrophy
ClinicalTrials.gov Identifier: NCT00167609 - Completed
Myotonic Dystrophy
- Levetiracetam for Cramps, Spasticity and Neuroprotection in Motor Neuron Disease
ClinicalTrials.gov Identifier: NCT00324454 - Active, not recruiting
Motor Neuron Disease; Amyotrophic Lateral Sclerosis; Primary Lateral Sclerosis; Progressive Muscular Atrophy
- TOM: Testosterone in Older Men With Sarcopenia
ClinicalTrials.gov Identifier: NCT00240981 - Recruiting
Sarcopenia; Hypogonadism; Muscular Diseases
- Relatively healthy male veterans observed over time to see what types of diseases develop
ClinicalTrials.gov Identifier: NCT00076141 - Active, not recruiting
Healthy
- Phase 1 Pilot Study of 4-MP to Treat Stargardt Macular Dystrophy
ClinicalTrials.gov Identifier: NCT00346853 - Completed
Stargardt Macular Dystrophy
- Studies in Families With Corneal Dystrophy or Other Inherited Corneal Diseases
ClinicalTrials.gov Identifier: NCT00357435 - Recruiting
Corneal Dystrophies, Hereditary; Corneal Disease
- Phase II Study of Leuprolide and Testosterone for Men with Kennedy's Disease or Other Motor Neuron Disease
ClinicalTrials.gov Identifier: NCT00004771 - Completed
Spinal Muscular Atrophy; Amyotrophic Lateral Sclerosis; Spinobulbar Muscular Atrophy
- Study of Safety and Dosing Effect on SMN Levels of Valproic Acid (VPA) in Patients With Spinal Muscular Atrophy
ClinicalTrials.gov Identifier: NCT00374075 - Completed
Spinal Muscular Atrophy
- Study of the Effects of Muscular Activity on Iron Metabolism
ClinicalTrials.gov Identifier: NCT00378469 - Recruiting
Iron Overload; Iron Deficiency
- Comparison of Two Types of Biopsy in Patients With Breast Lesions That Cannot Be Felt Upon Examination
ClinicalTrials.gov Identifier: NCT00006031 - Active, not recruiting
Breast Cancer
- Trial to Assess Safety, Tolerability, and Immunogenicity of Influenza Virus Vaccine, Trivalent, Types A & B, Live Cold-Adapted (FluMist) and Measles, Mumps, Rubella, and Varicella Vaccines Administered Concurrently to Healthy Children
ClinicalTrials.gov Identifier: NCT00192491 - Active, not recruiting
Influenza
- Comparative Trial Between 3 Types of Insulin Infusion Protocols
ClinicalTrials.gov Identifier: NCT00582309 - Recruiting
Hyperglycemia
- A Study of the Clinicopathologic Behaviour of the Different Types of Unsafe Chronic Otitis Media
ClinicalTrials.gov Identifier: NCT00270660 - Active, not recruiting
Chronic Otitis Media; Cholesteatoma
- Study of Coronary Artery Disease by Two Types of Angiography
ClinicalTrials.gov Identifier: NCT00273819 - Recruiting
Congestive Heart Failure
- Comparing the Effectiveness of Three Types of Therapy for the Treatment of Anorexia Nervosa in Adolescents
ClinicalTrials.gov Identifier: NCT00183586 - Recruiting
Eating Disorders
- Concomitant Use of Gardasil (V501, Human Papillomavirus [Types 6, 11, 16, 18] Recombinant Vaccine) With Combined Diphtheria, Tetanus, Pertussis Vaccine and Meningococcal Conjugate Vaccine in Adolescents
ClinicalTrials.gov Identifier: NCT00325130 - Active, not recruiting
Neoplasms, Glandular and Epithelial; Diphtheria; Tetanus; Whooping Cough; Meningitis
- Concomitant Use of Gardasil (V501, Human Papillomavirus [Types 6, 11, 16, 18] Recombinant Vaccine) With Combined Diphtheria, Tetanus, Pertussis and Poliomyelitis Vaccine in Adolescents
ClinicalTrials.gov Identifier: NCT00337428 - Active, not recruiting
Neoplasms, Glandular and Epithelial; Diphtheria; Tetanus; Whooping Cough; Poliomyelitis
- A Comparison Between Full Thickness and Partial Thickness Corneal Transplantation for Corneal Edema
ClinicalTrials.gov Identifier: NCT00346138 - Recruiting
Fuch's Dystrophy; Corneal Edema
- Comparison of Two Under Knee Lower Limb Bypass Types:Endothelialised Prosthesis Versus Autologous Vein Graft
ClinicalTrials.gov Identifier: NCT00221806 - Recruiting
Arteritis
- Study of Novel Types of Familial Diabetes Insipidus
ClinicalTrials.gov Identifier: NCT00004364 - Active, not recruiting
Diabetes Insipidus
- A Study to Compare the Efficacy and Safety of Two Different Types of Botulinum Toxin Type A in the Treatment of Moderate to Severe Cervical Dystonia
ClinicalTrials.gov Identifier: NCT00432341 - Recruiting
Spasmodic Torticollis
- Pilot Study of Growth Hormon to Treat SMA Typ II and III
ClinicalTrials.gov Identifier: NCT00533221 - Not yet recruiting
Muscular Atrophy, Spinal
- A Research Study to Test (2) Two Different Types of Feeding Tubes Used in the Intensive Care Unit
ClinicalTrials.gov Identifier: NCT00245687 - Recruiting
no Primary Disease; ICU Patient Who Require Enteral Nutrition
- Mouse Cancer Cell-Containing Macrobeads in the Treatment of Human Cancer
ClinicalTrials.gov Identifier: NCT00283075 - Recruiting
Intraabdominal Cancers (Various Types)
- Functional Dyspepsia - Effect of Acid-Reducing Treatment and Information on Various Types of Dysmotility
ClinicalTrials.gov Identifier: NCT00437346 - Recruiting
Dyspepsia
- Effect Pulsatile IV Insulin Therapy on the Quality of Life in Patients With Types 1 and 2 Diabetes
ClinicalTrials.gov Identifier: NCT00228878 - Recruiting
Diabetes Mellitus
- Effect of DHA Supplements on Macular Function in Patients with Stargardt Macular Dystrophy and Stargardt-like Macular Dystrophy
ClinicalTrials.gov Identifier: NCT00060749 - Completed
Macular Degeneration
- Effectiveness of Two Types of Treatment in Restoring Muscle After Hip Surgery
ClinicalTrials.gov Identifier: NCT00393848 - Recruiting
Hip Fracture; Osteoarthritis; Femur Head Necrosis
- Physiologic Effects of PRMS & Testosterone in the Debilitated Elderly
ClinicalTrials.gov Identifier: NCT00018356 - Completed
Muscle Weakness; Muscular Atrophy
- Imatinib Mesylate in Patients With Various Types of Malignancies Involving Activated Tyrosine Kinase Enzymes
ClinicalTrials.gov Identifier: NCT00171912 - Recruiting
Hypereosinophilic Syndrome; Systemic Mastocytosis; Chronic Myelomonocytic Leukemia; Dermatofibrosarcoma
- A Study of MORAb-009 in Subjects With Pancreatic Cancer, Mesothelioma, or Certain Types of Ovarian or Lung Cancer
ClinicalTrials.gov Identifier: NCT00325494 - Active, not recruiting
Pancreatic Cancer; Mesothelioma; Ovarian Cancer; Non-Small Cell Lung Cancer
- Three Different Types of Thermometers in Measuring Temperature in Young Patients With Fever and Without Fever
ClinicalTrials.gov Identifier: NCT00378846 - Recruiting
Fever, Sweats, and Hot Flashes
- Effects of exercise on markers of inflammation in skeletal muscle in elderly hip fracture patients
ClinicalTrials.gov Identifier: NCT00006194 - Completed
Hip Fractures; Muscular Atrophy
- Muscular Strengthening for Paretic Knee Flexor and Extensor by Conventional Physiotherapy on Chronic Hemiplegic Stroke Patients
ClinicalTrials.gov Identifier: NCT00570570 - Not yet recruiting
Hemiplegia; Stroke
- Effects of Pulsatile Insulin Delivery on Diabetic Neuropathy in Patients With Types 1 and 2 Diabetes Mellitus
ClinicalTrials.gov Identifier: NCT00228891 - Recruiting
Diabetes Mellitus, With Complications
- Comparison of Different Types of Surgery in Treating Patients With Stage IA Non-Small Cell Lung Cancer
ClinicalTrials.gov Identifier: NCT00499330 - Recruiting
Lung Cancer
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