Rare Diseases Treatment and Symptoms
Rare Diseases Articles
- Gene Therapy for Cancer: Questions and Answers
... Key Points Gene therapy is an experimental treatment that involves introducing genetic material into a person’s cells to fight disease (see Question 2). Researchers are studying gene therapy for...
- About the Human Genome Project (National Human Genome Research Institute)
- FDA Fights Rare Diseases: New Help for Patients without Treatments (Food and Drug Administration)