Cystic Fibrosis |
CF; Cystic Fibrosis Research Directions; Fibrocystic Disease of Pancreas; Mucoviscidosis |
Cystic fibrosis (CF) is a common hereditary disease that affects the entire body, causing progressive disability and early death. Breathing difficulties are the most common symptom and result from frequent lung infections, which are treated, though not always cured, by antibiotics and other medications. CF is a multi-system disorder of exocrine glands causing the formation of a thick mucus substance that affects the lungs, intestines, pancreas, and liver. The standard test for diagnosis is ...
Wikipedia - [full article]
Cystic Fibrosis Clinical Trials
- Can Quantitative Ultrasound Be Used for the Evaluation of Bone Health in Adolescents and Adults with Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00221572 - Recruiting
Cystic Fibrosis
- Study of Total Energy Expenditure in Infants and Children With Moderate to Severe Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00006273 - Active, not recruiting
Cystic Fibrosis
- Study of Hepatic Glucose Production and De novo Lipogenesis in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00014781 - Recruiting
Cystic Fibrosis
- A Study to Evaluate Nutropin AQ for the Treatment of Growth Restriction in Children with Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00079742 - Active, not recruiting
Cystic Fibrosis
- Behavioral & Nutritional Treatment to Help CF Preschoolers Grow
ClinicalTrials.gov Identifier: NCT00241969 - Recruiting
Cystic Fibrosis; Pancreatic Cystic Fibrosis
- Quantification of pulmonary neutrophil activity in cystic fibrosis using radiolabeled fluorodeoxyglucose and PET imaging
ClinicalTrials.gov Identifier: NCT00023465 - Recruiting
Cystic Fibrosis
- Tissue Collection from People with Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00015756 - Active, not recruiting
Cystic Fibrosis
- Zinc Homeostasis and Kinetics in Children with Cystic Fibrosis (CF)
ClinicalTrials.gov Identifier: NCT00104494 - Recruiting
Cystic Fibrosis
- Comparison of Inhaled Mannitol and rhDNase in Children with Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00117208 - Active, not recruiting
Cystic Fibrosis
- A Pilot Trial of Phenylbutyrate/Genistein Duotherapy (for Cystic Fibrosis)
ClinicalTrials.gov Identifier: NCT00016744 - Recruiting
Cystic Fibrosis
- Effect of Lubiprostone on Nutritional Status and Pulmonary Function in Adults With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00577499 - Enrolling by invitation
Cystic Fibrosis; Constipation; Nutrition
- Phase I Pilot Study of Gene Therapy for Cystic Fibrosis Using Cationic Liposome Mediated Gene Transfer
ClinicalTrials.gov Identifier: NCT00004471 - Active, not recruiting
Cystic Fibrosis
- Study of Denufosol Inhalation Solution in Patients With Mild Cystic Fibrosis Lung Disease
ClinicalTrials.gov Identifier: NCT00357279 - Active, not recruiting
Cystic Fibrosis
- Randomized Study of Alendronate in Adult Patients With Cystic Fibrosis Related Osteoporosis
ClinicalTrials.gov Identifier: NCT00004489 - Recruiting
Osteoporosis; Cystic Fibrosis
- Efficacy and Safety of 28 or 56 Days Treatment With Inhaled Tobramycin Nebuliser Solution for Pseudomonas Aeruginosa Infection in Children With Cystic Fibrosis.
ClinicalTrials.gov Identifier: NCT00391976 - Active, not recruiting
Cystic Fibrosis
- Growth Hormone Treatment Study in Children With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00256555 - Active, not recruiting
Cystic Fibrosis
- Safety Study of Aztreonam Lysinate for Inhalation (AI) in Cystic Fibrosis Patients with P. Aeruginosa
ClinicalTrials.gov Identifier: NCT00128492 - Active, not recruiting
Cystic Fibrosis
- Macrolide Antibiotic Therapy for Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00205634 - Active, not recruiting
Cystic Fibrosis
- Growth Hormone Use in Adolescents and Adults With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00287430 - Active, not recruiting
Cystic Fibrosis
- Metabolic Abnormalities in Hispanic Children With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00287443 - Active, not recruiting
Cystic Fibrosis
- Influence of DHA-Rich Supplement on DHA-Status and Health Evolution of Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00221546 - Active, not recruiting
Cystic Fibrosis
- Study of Denufosol Inhalation Solution in Patients With Mild to Moderate Cystic Fibrosis Lung Disease
ClinicalTrials.gov Identifier: NCT00425165 - Recruiting
Cystic Fibrosis
- Effectiveness of Pulmozyme in Infants With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00179998 - Active, not recruiting
Cystic Fibrosis
- Safety and Efficacy of PTC124 for Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00237380 - Active, not recruiting
Cystic Fibrosis
- Pharmacokinetic Study of Lansoprazole in Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00458614 - Active, not recruiting
Cystic Fibrosis
- Long Term Administration of Inhaled Dry Powder Mannitol In Cystic Fibrosis - A Safety and Efficacy Study
ClinicalTrials.gov Identifier: NCT00446680 - Recruiting
Cystic Fibrosis
- Phase II Study of the Safety and Efficacy of Inhaled Alpha-1 Antitrypsin (AAT ) in Cystic Fibrosis Patients
ClinicalTrials.gov Identifier: NCT00499837 - Recruiting
Cystic Fibrosis
- Evaluation of a Decision Aid for Adult Cystic Fibrosis Patients Considering Bilateral Lung Transplantation
ClinicalTrials.gov Identifier: NCT00345449 - Recruiting
Cystic Fibrosis
- 18FDG- PET/CT Contribution to the Assessment of Lesion Severity in Cystic Fibrosis (CF)
ClinicalTrials.gov Identifier: NCT00363402 - Recruiting
Cystic Fibrosis
- Evaluation of the Safety and Efficacy of Pancrecarb® MS-16 in Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00432861 - Recruiting
Cystic Fibrosis; Pancreatic Insufficiency
- The Prevalence and Significance of Gastro-Oesophageal Reflux in Cystic Fibrosis Before and After Lung Transplantation
ClinicalTrials.gov Identifier: NCT00164021 - Recruiting
Cystic Fibrosis
- Assessment of Quadriceps Muscle Electrostimulation Used in Patients Suffering From Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00391703 - Recruiting
Cystic Fibrosis; Mucoviscidosis
- The Short Term Safety and Efficacy of Inhaled L-Arginine in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00405665 - Recruiting
Cystic Fibrosis
- Prolonging the Duration of Peripheral Venous Catheters in Cystic Fibrosis People
ClinicalTrials.gov Identifier: NCT00418470 - Recruiting
Cystic Fibrosis; Phlebitis
- Safety, Pharmacokinetic and Pharmacodynamic Study of MP-376 in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00503490 - Recruiting
Cystic Fibrosis
- Evaluation of the Emission Distance of P. Aeruginosa From the Respiratory Tract of People With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00531531 - Recruiting
Cystic Fibrosis
- Multidose Safety and Tolerability Study of (Arikaceâ„¢) for Inhalation In Cystic Fibrosis Patients
ClinicalTrials.gov Identifier: NCT00558844 - Recruiting
Cystic Fibrosis
- Genetic Modifiers of Cystic Fibrosis: Sibling Study
ClinicalTrials.gov Identifier: NCT00037778 - Recruiting
Lung Diseases; Cystic Fibrosis
- Study of Tauroursodeoxycholic Acid for Hepatobiliary Disease in Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00004441 - Recruiting
Cystic Fibrosis
- Study of Alendronate to Prevent and Treat Osteoporosis in Cystic Fibrosis Patients
ClinicalTrials.gov Identifier: NCT00157690 - Active, not recruiting
Cystic Fibrosis; Osteoporosis; Bone Diseases, Metabolic
- A Phase I Study of Inhaled Sodium Pyruvate for the Treatment of Cystic Fibrosis.
ClinicalTrials.gov Identifier: NCT00332215 - Recruiting
Cystic Fibrosis
- Efficacy and Safety Study of Inhaled Glutathione in Cystic Fibrosis Patients
ClinicalTrials.gov Identifier: NCT00506688 - Recruiting
Cystic Fibrosis
- Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of QAU145 in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00506792 - Recruiting
Cystic Fibrosis
- Treatment of Aspergillus Fumigatus (a Fungal Infection) in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00528190 - Recruiting
Cystic Fibrosis
- Safety and Tolerability of Inhaled Nitric Oxide in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00570349 - Recruiting
Cystic Fibrosis
- Gene Modifiers in Cystic Fibrosis Lung Disease
ClinicalTrials.gov Identifier: NCT00037765 - Active, not recruiting
Cystic Fibrosis; Lung Diseases
- Increased Gluconeogenesis is One Cause of Cystic Fibrosis Related Diabetes (CFRD)
ClinicalTrials.gov Identifier: NCT00082238 - Recruiting
Cystic Fibrosis; Diabetes Mellitus
- A Study in Pediatric Patients with Cystic Fibrosis Lung Disease
ClinicalTrials.gov Identifier: NCT00130182 - Completed
Cystic Fibrosis
- Treatment of Metabolic Alkalosis in Acute Exacerbations of Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00163852 - Recruiting
Cystic Fibrosis
- Safety Study of VX 770 in Subjects With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00457821 - Recruiting
Cystic Fibrosis
- Tolerability of Inhaled Hypertonic Saline in Infants With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00546663 - Recruiting
Cystic Fibrosis
- Non-Invasive Ventilation and Oxygen Therapy in Cystic Fibrosis Patients with Nocturnal Oxygen Desaturation
ClinicalTrials.gov Identifier: NCT00157183 - Recruiting
Cystic Fibrosis
- Phase II Pilot Study to Compare the Bioavailability of Buffered, Enteric-Coated Ursodiol with Unmodified Ursodiol for Chronic Cholestatic Liver Disease and Cystic Fibrosis-Associated Liver Disease
ClinicalTrials.gov Identifier: NCT00004315 - Active, not recruiting
Cystic Fibrosis; Gastrointestinal Diseases; Cholestasis
- Use of the Insulin Pump in Cystic Fibrosis Patients With Impaired Glucose Tolerance or CFRD and in Type 1 Diabetes Patients.
ClinicalTrials.gov Identifier: NCT00287456 - Active, not recruiting
Cystic Fibrosis Related Diabetes
- Mannitol Dose Response Study in Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00251056 - Recruiting
Cystic Fibrosis
- Inhaled Sodium Pyruvate for the Treatment of Cystic Fibrosis.
ClinicalTrials.gov Identifier: NCT00308243 - Recruiting
Cystic Fibrosis
- Disclosing a Cystic Fibrosis Diagnosis to a Dating Partner
ClinicalTrials.gov Identifier: NCT00485082 - Recruiting
Cystic Fibrosis
- Use of Formula Fortified With DHA in Infants With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00530244 - Recruiting
Cystic Fibrosis
- Miglustat / OGT 918 in the Treatment of Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00537602 - Recruiting
Cystic Fibrosis
- Coping Compliance and Adjustment in Adolescents With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00577252 - Recruiting
Cystic Fibrosis
- Phase I Randomized Study of Adeno-Associated Virus-CFTR Vector in Patients with Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00004533 - Active, not recruiting
Cystic Fibrosis
- Nasal Inhalation of Dornase Alfa (Pulmozyme) in Patients With Cystic Fibrosis and Chronic Rhinosinusitis
ClinicalTrials.gov Identifier: NCT00265434 - Active, not recruiting
Cystic Fibrosis; Chronic Rhinosinusitis
- Phase II Study of Growth Hormone in Children With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00016445 - Active, not recruiting
Cystic Fibrosis
- Amiloride Solution and Tobramycin Solution for Inhalation for the Eradication of Burkholderia Dolosa in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00547053 - Recruiting
Cystic Fibrosis
- Improving Vitamin D Status In Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00450073 - Recruiting
Cystic Fibrosis
- PTC124 for Pediatric Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00458341 - Recruiting
Cystic Fibrosis
- Absorptive Clearance in the Cystic Fibrosis Airway
ClinicalTrials.gov Identifier: NCT00541190 - Recruiting
Cystic Fibrosis
- IGF-1 Therapy in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00566241 - Recruiting
Cystic Fibrosis
- Study Investigating a Delayed-Release Pancrelipase in Patients With Exocrine Pancreatic Insufficiency Due to Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00510484 - Not yet recruiting
Cystic Fibrosis
- Studying Patients with Cystic Fibrosis and Other Pulmonary and Pancreatic Disorders
ClinicalTrials.gov Identifier: NCT00001223 - Recruiting
Bronchiectasis; Cystic Fibrosis; Pancreatic Insufficiency
- Phase I Study of Liposome-Mediated Gene Transfer in Patients with Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00004806 - Completed
Cystic Fibrosis
- Study of INS37217 Inhalation Solution in Mild to Moderate Cystic Fibrosis Lung Disease
ClinicalTrials.gov Identifier: NCT00056147 - Completed
Cystic Fibrosis
- Nasal Inhalation of Pulmozyme in Patients With Cystic Fibrosis and Chronic Rhinosinusitis
ClinicalTrials.gov Identifier: NCT00534079 - Recruiting
Cystic Fibrosis; Rhinosinusitis
- Nutritional, Metabolic and Respiratory Status in Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00476281 - Not yet recruiting
Cystic Fibrosis; Diabetes
- The Effect of rhDNase on Ventilation Inhomogeneity in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00557089 - Not yet recruiting
Cystic Fibrosis
- Efficacy and Safety of ULTRASE MT20 in Improving the Coefficient of Fat Absorption (CFA%) in Children With Cystic Fibrosis (CF) and Pancreatic Insufficiency (PI)
ClinicalTrials.gov Identifier: NCT00513682 - Recruiting
Cystic Fibrosis; Pancreatic Insufficiency
- A Trial of Pulmozyme Withdrawal on Exercise Tolerance in Cystic Fibrosis Subjects With Severe Lung Disease (TOPIC)
ClinicalTrials.gov Identifier: NCT00434278 - Recruiting
Cystic Fibrosis; Lung Disease
- Phase I Pilot Study of Ad5-CB-CFTR, an Adenovirus Vector Containing the Cystic Fibrosis Transmembrane Conductance Regulator Gene, in Patients with Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00004779 - Completed
Cystic Fibrosis
- 8-Day Safety, Tolerability, and Effects Study of Inhaled INS37217 and Placebo In Adult and Pediatric Cystic Fibrosis Patients
ClinicalTrials.gov Identifier: NCT00034515 - Completed
Cystic Fibrosis
- Capsule Endoscopy in Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00333957 - Recruiting
Cystic Fibrosis
- PTC124 for Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00234663 - Active, not recruiting
Cystic Fibrosis
- Study of Uridine Triphosphate (UTP) as an Aerosol Spray for Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00004705 - Completed
Cystic Fibrosis
- Prevalence and Treatment of Urinary Incontinence in Women With Cystic Fibrosis and Chronic Obstructive Pulmonary Disease
ClinicalTrials.gov Identifier: NCT00164138 - Active, not recruiting
Cystic Fibrosis; Chronic Obstructive Pulmonary Disease (COPD)
- Nasally Delivered Pulmozyme for Sinusitis in Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00416182 - Recruiting
Sinusitis; Cystic Fibrosis
- Safety of Tobramycin Inhalation Powder (TIP) vs Tobramycin Solution for Inhalation in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00388505 - Recruiting
Cystic Fibrosis
- Scandinavian Cystic Fibrosis Azithromycin Study
ClinicalTrials.gov Identifier: NCT00411736 - Not yet recruiting
Cystic Fibrosis
- Study of Ibuprofen to Preserve Lung Function in Patients with Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00004440 - Completed
Cystic Fibrosis
- Randomized Study of Pancrelipase With Bicarbonate (PANCRECARB) Capsules in Reducing Steatorrhea in Patients With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00006063 - Completed
Cystic Fibrosis
- Study of Denufosol Tetrasodium in Patients with Cystic Fibrosis Lung Disease
ClinicalTrials.gov Identifier: NCT00103714 - Completed
Cystic Fibrosis
- A Study of the Safety and Efficacy of Tobramycin for Inhalation in Young Children with Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00006280 - Completed
Cystic Fibrosis
- Role of Toxins in Lung Infections Caused by Pseudomonas Aeruginosa
ClinicalTrials.gov Identifier: NCT00027183 - Recruiting
Pseudomonas Infection; Cystic Fibrosis
- An Effectiveness, Safety, and Palatability Study of Pancrelipase Microtablets in Infants and Toddlers With Cystic Fibrosis and Fat Malabsorption
ClinicalTrials.gov Identifier: NCT00217204 - Completed
Steatorrhea; Cystic Fibrosis
- Growth Hormone Use in Cystic Fibrosis - a Multicenter Study
ClinicalTrials.gov Identifier: NCT00005112 - Completed
Cystic Fibrosis
- Phase I Randomized Study of CPX for the Treatment of Adult Patients with Mild Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00004428 - Completed
Cystic Fibrosis
- ALTU-135 Efficacy Trial in Patients With Cystic Fibrosis-Related Exocrine Pancreatic Insufficiency
ClinicalTrials.gov Identifier: NCT00449878 - Recruiting
Cystic Fibrosis; Exocrine Pancreatic Insufficiency
- A Study to Evaluate the Safety and Efficacy of Eurand Pancreatic Enzyme Product (PEP) in Patients With Cystic Fibrosis and Exocrine Pancreatic Insufficiency
ClinicalTrials.gov Identifier: NCT00297167 - Recruiting
Cystic Fibrosis; Exocrine Pancreatic Insufficiency
- Study of Metabolic Effects of Pregnancy in Women With Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00014768 - Terminated
Cystic Fibrosis
- Bone Health of People with Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00008762 - Completed
Cystic Fibrosis
- Early Pseudomonas Infection Control (EPIC) Trial
ClinicalTrials.gov Identifier: NCT00097773 - Recruiting
Cystic Fibrosis; Infection; Lung Diseases
- Hydroxychloroquine in Cystic Fibrosis
ClinicalTrials.gov Identifier: NCT00311883 - Recruiting
Cystic Fibrosis
Resources
- (National Women's Health Information Center, OWH, HHS)
- Ask NOAH About: Cystic Fibrosis (National Organization for Albinism and Hypopigmentation)

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